Medical Affairs

Congress posters & Presentations

Congress materials from Beren-sponsored research

Poster
Survival Analysis
Poster: A target trial emulation framework for externally controlled survival analyses ininfantile-onset Niemann-Pick disease type C

October 26, 2026

NORD Breakthrough Summit 2026
Poster
Biomarkers
NPCCSS
Survival Analysis
Poster: Efficacy of Intrathecal Adrabetadex in Infantile-Onset Niemann-Pick Disease Type C is Supported by Survival, Clinical, and Biomarker Data

October 26, 2026

NORD Breakthrough Summit 2026
Poster
Poster: Case Report of Siblings With Infantile-Onset Niemann-Pick Type C (I-NPC) Initiating Adrabetadex at Different Ages and Intervals From Disease Onset

October 14, 2026

Child Neurology Society Annual Meeting 2026
Poster
NPCCSS
Survival Analysis
Poster: Survival outcomes by baseline disease burden in participants with infantile-onset Niemann-Pick disease type C treated with adrabetadex

October 14, 2026

Child Neurology Society Annual Meeting 2026
Poster
NPCCSS
Poster: Outcomes in participants with infantile-onset Niemann-Pick disease type C receiving prompt and sustained treatment with adrabetadex

October 14, 2026

Child Neurology Society Annual Meeting 2026
Poster
Poster: Early evidence of an emerging NPC treatment paradigm: adrabetadex use alongside arimoclomol and/or levacetylleucine

October 14, 2026

Child Neurology Society Annual Meeting 2026
Poster
NPCCSS
Survival Analysis
Poster: Survival outcomes by baseline disease burden in participants with infantile-onset Niemann-Pick disease type C treated with adrabetadex

May 31, 2026

Ara Parseghian Medical Research Fund 2026
Poster
NPCCSS
Poster: Outcomes in participants with infantile-onset Niemann-Pick disease type C receiving prompt and sustained treatment with adrabetadex

May 31, 2026

Ara Parseghian Medical Research Fund 2026
Poster
Poster: Early evidence of an emerging NPC treatment paradigm: adrabetadex use alongside arimoclomol and/or N‑acetyl‑L‑leucine

May 31, 2026

Ara Parseghian Medical Research Fund 2026
Poster
Preclinical
Poster: Adrabetadex alone or in combination with arimoclomol and levacetylleucine promotes oligodendrocyte proliferation, synaptic network growth, and myelination in an in vitro mouse model of Niemann-Pick disease type C

May 31, 2026

Ara Parseghian Medical Research Fund 2026

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The information provided on this website is provided by the Beren Therapeutics P.B.C. (“Beren”) Medical Affairs team for healthcare professionals in the US. It is designed to provide self-service access to medical information and medical affairs content about Beren products, pipeline, and therapeutic areas of interest including clinical data, research developments, congress materials, and publications. Certain materials such as posters and presentations presented in this website are a result of Beren-sponsored research and are not intended to be a comprehensive overview of all information and materials presented at a particular congress. The website is intended to provide scientifically balanced information and educational resources and may include information related to products or indications that have not been approved by the US Food and Drug Administration. The information provided is not intended as medical advice and does not replace independent medical judgement. By searching this website, you confirm the unsolicited nature of your inquiry. Please confirm that you agree and that you are a registered healthcare professional registered to practice in the US.

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