Poster: Early evidence of an emerging NPC treatment paradigm: adrabetadex use alongside arimoclomol and/or levacetylleucine
Citation: Berry-Kravis E, et al. Early evidence of an emerging NPC treatment paradigm: adrabetadex use alongside arimoclomol and/or levacetylleucine. Poster presented at: Child Neurology Society Annual Meeting; October 2026.